Deanna Portero 12/15/25 Deanna Portero 12/15/25

Fondazione Telethon and Orphan Therapeutics Accelerator Sign Memorandum of Understanding to Pioneer Non-Profit Commercial Access Model for Ultra-Rare Disease Gene Therapy in the US

Dean A. Wetherbee 8/12/25 Dean A. Wetherbee 8/12/25

Orphan Therapeutics Accelerator Launches Orphan Therapies, a Non-Profit Biotech Dedicated to Commercializing Ultra-Rare Disease Treatments

Orphan Therapeutics Accelerator (OTXL), a non-profit organization focused on advancing shelved ultra-rare disease treatments through clinical trials, today announced the launch of its wholly owned subsidiary, Orphan Therapies (OT) LLC. Orphan Therapies will focus on commercializing and providing sustained, equitable patient access to approved therapies for conditions with very small patient populations.